We have written about the promise of gene therapy to correct genetic disease many times. An exciting development happened ...

Meanwhile, ARK sold 15,362 shares of Roku Inc (NASDAQ:ROKU) through its ARKK ETF, totaling $1,668,774. This marks a continuation of ARK’s recent trend of reducing its holdings in the streaming ...

NEW YORK – Azalea Therapeutics launched on Tuesday, having raised $82 million in seed and Series A financing to develop in vivo genetic medicines for cancer and autoimmune conditions using its ...

In a bid to help children suffering from a rare and life-threatening genetic disorder, Member of Parliament from Delhi’s Chandni Chowk, Praveen Khandelwal, has written to Prime Minister Narendra Modi, ...

The grantmaking organization Open Philanthropy has awarded funding for a University of California San Diego technology ...

Recognized in the Biotechnology category of the 2025 Top Innovations contest, small Cas12l nucleases are versatile, ...

CRISPR technology could one day create “designer babies, ” raising major ethical and social inequality concerns.

In a world first, a bespoke gene-editing therapy benefited one child. Now researchers plan to launch a clinical trial of the approach ...

First company to enable precision in vivo genome engineering, combining both cell-specific delivery and programmable, locus-specific gene insertion, with the potential to achieve physiological, ...

We’ve gone from asking, “How can we afford to make more videos?” to “How do we make sure the ones we already made are ...

A new West Coast biotech has emerged into the busy in vivo cell therapy space, this time with the backing of Nobel Prize-winning CRISPR pioneer Jennifer Doudna, Ph.D. Azalea Therapeutics has bloomed ...

LAMA2-CMD is among the world’s rarest and most devastating genetic disorders, affecting infants and young children, often depriving them of the ability to walk, move, or even breathe independently.