Inc. (Nasdaq: BEAM), a biotechnology company developing precision genetic medicines through base editing, today announced that the company will present updated safety and efficacy data from the BEACON ...
Recently approved by the European Medicines Agency, RESTORE will evaluate iadademstat’s ability to raise fetal hemoglobin (HbF) in adult patients ...
Amy Cohen is running the New York City Marathon despite living with the painful effects of sickle cell disease.
For patients, every encounter is a test not just of the healthcare system, but of whether they are believed and respected.
Patients with sickle cell disease and beta-thalassemia treated with exagamglogene autotemcel reported substantial and ...
Thousands of Californians live with sickle cell disease, a painful blood disorder. But new treatments, including a promising form of gene therapy, are offering hope to ...
Life expectancy has soared and interest in the disease is growing, but breakthrough gene therapies are extraordinarily ...
"The data we’re presenting at this year’s ASH meeting reflect the strong momentum of our in vivo programs for sickle cell disease (SCD) and T-cell engineering,” said Michael Severino, M.D., CEO of ...
NYU researchers partnered with Nigerian singer Adekunle Gold to launch an organization that uses music to reduce stigma and ...
After years of battling sickle cell and repeated hospital stays, Shablinah Nazziwa rose to become Uganda Christian University’s overall best graduate with a Cumulative Grade Point Average ...
Nollywood actor and model, Emmanuel Ikubese has taken his craft a notch higher, producing and directing a movie titled Mzigo ...