In 2013, Benjamin Oakes was hellbent on getting his PhD while working on the bleeding edge of molecular engineering: refining a gene editing tool, Crispr, that promised to some day cut DNA as ...

Caribou Biosciences shares rose after its CAR-T therapies showed high response rates and durable remissions in lymphoma and myeloma trials.

Cutting-edge gene editing technology could eradicate Down syndrome, according to Japanese scientists. Down syndrome, which causes a range of developmental differences and affects 1 in 700 newborns in ...

OF THE MANY patients who need an organ from a donor, 90% go without. About 240m people live with rare genetic diseases, most of which cannot be treated. Each year poor diets cause more than 10m early ...

A lthough still in its early days, CRISPR has already been called the most powerful scientific tool of the century. Using ...

On Friday, the U.S. Food and Drug Administration (FDA) approved a pair of gene therapies for the painful and potentially fatal blood disorder, sickle cell disease (SCD)–including the first-ever CRISPR ...

The world's first patient to be treated with personalized gene editing therapy is finally headed home after over 300 days in the hospital. Nine-month-old KJ Muldoon recently underwent CRISPR-based ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

WEST LAFAYETTE, Ind. — More than a decade ago, scientists harnessed a bacterial molecular machine that identifies and cuts specific sections of DNA, revolutionizing the ability to edit genes and ...

Please provide your email address to receive an email when new articles are posted on . In an early study, a gene-editing therapy drastically reduced levels of transthyretin, the protein that causes ...