A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two years after the treatment.
The Boston biotech founded by Harvard professor David Sinclair is testing whether cellular reprogramming can turn back the ...
UniQure's therapy, called AMT-130, reduced disease progression by 75% at 36 months in patients who received a high dose.
The Chosun Ilbo on MSN
FDA Speeds Up Custom Gene Therapy Approvals With Existing Data
Last May, people were thrilled to learn that a 7-month-old baby who became the first in the world to receive a personalized ...
In a first for adults in Singapore, scientists are conducting gene editing trials on heart patients to correct defects at ...
Researchers announce breakthrough results for AMT-130, the first disease-modifying treatment for Huntington's disease, with ...
Intellia earlier this year reported a similar grade 4 liver enzyme elevation associated with the gene therapy nexiguran ...
The FDA has officially placed two of Intellia’s Phase III studies under clinical hold after the biotech reported earlier this ...
ABC 11 Raleigh, NC on MSN
Duke Eye Center pioneers new gene therapy for rare eye disease
Duke Eye Center has become the first academic medical center in the country to implant a new cell-based gene therapy for a ...
In honor of World Blindness Awareness Month, "GMA" is spotlighting a breakthrough gene therapy that's helping some blind ...
Oncologists' experience with CGT has increased, with more patients treated and earlier lines of therapy being utilized.
Some of the most expensive drugs currently in use are gene therapies to treat specific diseases, and their high cost limits ...
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